Niemann–Pick type C disease: cellular pathology and pharmacotherapy - Wheeler - 2020 - Journal of Neurochemistry - Wiley Online Library
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Contribution of ceramides metabolism in psychiatric disorders
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Niemann–Pick Disease Type C: Induced Pluripotent Stem Cell–Derived
Quantitative proteomic analysis of Rett iPSC-derived neuronal
Niemann-Pick type C disease (NPC) - ScienceDirect
Contribution of ceramides metabolism in psychiatric disorders
Tolerance of chronic HDACi treatment for neurological, visceral
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